Leukodystrophies - from diagnosis towards mechanistic understanding and treatment 

Friday May 23 2025

Location: Vrije Universiteit Amsterdam (VU) - Auditorium

08.30 - 09.00 Envisioning the development of therapautic modalities - Nicole Wolf
09.00 - 09.30 Envisioning the future of gene therapy - Niek van Til
09.30 - 10.00 Molecular targets for therapy - Truus Abbink
10.00 - 10.30 Clinical outcome measures - Marc Engelen
10.30 - 11.00 Tea and coffee
11.00 - 12.30 Proffered papers on leukodystrophies
12.30 - 13.30 Lunch 
13.30 - 13.50 Registries for leukodystrophies and trial readiness - Daphne Schoenmakers
13.50 - 14.10 The interface between medical researchers and industry - Prisca Leferink
14.10 - 14.30 Prices for therapies - Carla Hollak
14.30 - 14.50 Leukodystrophies: a field of collaboration - Ali Fatemi
14.50 - 15.00  Closing - Nicole Wolf
 
 Location Vrije Universiteit (VU) - Aula
 
15.45 - 16.30 Farewell lecture (in Dutch) - Marjo van der Knaap
  Reception